A consortium of scientists, industry stakeholders, and patient advocacy leaders working together to promote advances in the diagnosis and treatment of leukodystrophies.
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Participants make it possible for researchers to find new treatments, speed diagnosis, and improve the lives of those affected by rare diseases.
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Rare Research Report: July 2025
Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for July 2025.
Pre-Doc Preparatory Program (P³) in Translational Research
Do you have a rare disease research coordinator, genetic counseling assistant, or technician who may benefit from formal training in clinical and translational research?
Rare Research Report: December 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.