A consortium of scientists, industry stakeholders, and patient advocacy leaders working together to promote advances in the diagnosis and treatment of leukodystrophies.
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Rare Research Report: February 2026
Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for February 2026.
Join the RDCRN for Rare Disease Day at NIH on February 27, 2026
Don’t miss the in-person and virtual celebration of Rare Disease Day at NIH on Friday, February 27, 2026, from 9 am to 5 pm EST.
Rare Research Report: November 2025
Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for November 2025.