A consortium of scientists, industry stakeholders, and patient advocacy leaders working together to promote advances in the diagnosis and treatment of leukodystrophies.
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Participants make it possible for researchers to find new treatments, speed diagnosis, and improve the lives of those affected by rare diseases.
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Rare Research Report: December 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.
Leukodystrophy Over Time: What We’re Learning from a Natural History Study
To learn more about the natural history of leukodystrophy, the Global Leukodystrophy Initiative Clinical Trials Network (GLIA-CTN) is conducting a study, “GLIA-CTN EHR Data Extraction Project.”
Rare Research Report: October 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.