A consortium of scientists, industry stakeholders, and patient advocacy leaders working together to promote advances in the diagnosis and treatment of leukodystrophies.
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Participants make it possible for researchers to find new treatments, speed diagnosis, and improve the lives of those affected by rare diseases.
Find a studyNIH Announces Funding to Establish and Strengthen Rare Disease Research Groups
The National Institutes of Health (NIH) has awarded approximately $26 million in grants in the fiscal year 2025 to begin the fifth cycle of funding for the Rare Diseases Clinical Research Network (RDCRN).
Rare Research Report: October 2025
Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for October 2025.
Rare Research Report: September 2025
Each month, we share summaries of recent Rare Diseases Clinical Research Network grant-funded publications. Catch up on RDCRN research for September 2025.