A consortium of scientists, industry stakeholders, and patient advocacy leaders working together to promote advances in the diagnosis and treatment of leukodystrophies.
Join one of our research studies
Participants make it possible for researchers to find new treatments, speed diagnosis, and improve the lives of those affected by rare diseases.
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Join the RDCRN for FDA-NIH Rare Disease Day, February 27-28, 2025
Don’t miss the in-person and virtual celebration of FDA-NIH Rare Disease Day on February 27-28, 2025.
Rare Research Report: December 2024
Each month, we share summaries of recent Rare Diseases Clinical Research Network (RDCRN) grant-funded publications.
Leukodystrophy Over Time: What We’re Learning from a Natural History Study
To learn more about the natural history of leukodystrophy, the Global Leukodystrophy Initiative Clinical Trials Network (GLIA-CTN) is conducting a study, “GLIA-CTN EHR Data Extraction Project.”
